Therapies that are available and under development for Duchenne muscular dystrophy: What about lung function?
Title | Therapies that are available and under development for Duchenne muscular dystrophy: What about lung function? |
Publication Type | Journal Article |
Year of Publication | 2020 |
Authors | Gogou, M., Pavlou E., & Haidopoulou K. |
Journal | Pediatr Pulmonol |
Volume | 55 |
Issue | 2 |
Pagination | 300-315 |
Date Published | 2020 02 |
ISSN | 1099-0496 |
Keywords | Glucocorticoids, Humans, Lung, Male, Morpholinos, Muscular Dystrophy, Duchenne, Prospective Studies, Quality of Life, Respiratory Function Tests, Ubiquinone |
Abstract | BACKGROUND: Respiratory failure is the principal source of morbidity and mortality among patients with Duchenne muscular dystrophy exerting a negative influence on their total quality of life. The aim of this review is to provide systematically current literature evidence about the effects of different treatment options (available or under development) for Duchenne muscular dystrophy on the pulmonary function of these patients. |
DOI | 10.1002/ppul.24605 |
Alternate Journal | Pediatr Pulmonol |
PubMed ID | 31834673 |